More than two years after the Government committed to adding SMA to newborn testing, families are still waiting ...

A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...

"Monumental" is how Ashley E. Webb, MD Assistant Professor, Department of Pediatrics, Division of Child & Adolescent Neurology Neuromuscular Program Director, UTHealth, University of Texas Health ...

A couple whose son died from a rare genetic condition are encouraging others to take part in screening which they say could ...

Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, ...

Spinal Muscular Atrophy, known as SMA Type 1, explained: A Paediatric neurologist shares insight into the condition after former Little Mix singer Jesy Nelson revealed her twins have been diagnosed ...

"Managing pain in patients with SMA begins with the recognition that there are predictable etiologies leading to pain in SMA and investigating them during each medical visit is important to implement ...

People with spinal muscle atrophy (SMA), an inherited neuromuscular disease, usually experience muscle weakness that impacts movement. New research suggests that electrical spinal cord stimulation ...

The singer shared an emotional update about her twins’ health on Sunday.

Former Little Mix singer Jesy Nelson is dealing with yet another heartbreaking truth. The singer and her longtime fiancé Zion Foster have called it quits. The unfortunate news comes just weeks after ...